Browsing: Gene

The US Food and Drug Administration’s Office of Therapeutic Products (OTP) convened a public listening session on September 18, 2025,…

Credit: vchal/Getty Images Researchers from Integra Therapeutics, in partnership with the Pompeu Fabra University (UPF) and the Center for Genomic…

Cirrus Therapeutics lands seed funding to advance gene therapy designed to prevent and reverse dry AMD by rejuvenating the retina.…

Credit: sorbetto/Getty Images French biotech EG 427 reports positive results from a trial of its gene therapy to target incontinence…

Universities must do more to prepare engineering students to manufacture cell and gene therapies, according to new analysis, which suggests…

Credit: Roger Harris / Science Photo Library/ Getty Images “What does the letter ‘E’ look like?” That was the response…

A gene therapy trial claims to show promising results for patients with Huntington’s disease. A press announcement of the experimental…

A brain scan of a person with Huntington’s disease, which causes a loss of brain volume as neurons are killed…

uniQure reported positive topline data from the pivotal Phase I/II study of AMT-130 for the treatment of Huntington’s disease. The…

Study highlights functional preservation in patients and signals the potential for pre-symptomatic intervention. For decades Huntington’s disease has stood as…