Browsing: Gene

A gene therapy trial claims to show promising results for patients with Huntington’s disease. A press announcement of the experimental…

A brain scan of a person with Huntington’s disease, which causes a loss of brain volume as neurons are killed…

uniQure reported positive topline data from the pivotal Phase I/II study of AMT-130 for the treatment of Huntington’s disease. The…

Study highlights functional preservation in patients and signals the potential for pre-symptomatic intervention. For decades Huntington’s disease has stood as…

Engineered prime editors display significantly improved edit to indel ratios, making them an attractive alternative for therapeutic applications.Image credit:©iStock, TanyaJoyPrime…

Credit: Stocktrek Images/Getty Images Canavan disease (CD) is a fatal genetic leukodystrophy caused by mutations in the ASPA gene, leading…

FUJIFILM Biosciences, a global leader in the innovation and manufacture of cell culture solutions for the Life Science market, today…

Cell culture media specialized for gene therapy production are uniquely designed to support the growth, viability, and productivity of cells used to…

Credit: ChrisChrisW / iStock / Getty Images Plus A child with a rare neurodevelopmental disorder died in a gene therapy…

DNA methylation is a key epigenome component that helps dictate how genes are expressed, contributing to normal cell and tissue…